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ADRXADARx Pharmaceuticals

美股Health Care2026-09-25

临床阶段生物技术公司,专注开发靶向肝脏的siRNA疗法治疗多种疾病。

$17发行价
$447M融资额
$19.35首日收盘
17.29%首日表现
临床阶段生物技术公司,专注开发靶向肝脏的siRNA疗法治疗多种疾病。
公司简介(来源:StockAnalysis)

ADARx Pharmaceuticals, Inc. operates as a clinical-stage biotechnology company that focuses on developing siRNA therapeutics to treat a broad spectrum of diseases. The company offers hepatic-targeted programs, including Agazisiran, a complement factor B (CFB) program that represents a pipeline-in-a-product opportunity, where a single therapeutic candidate has the potential to address multiple indications; Onvuzosiran, a clinical program for the prevention of HAE attacks; and ADX-626, a Factor XI (FXI) program for secondary stroke prevention wit...

生物医药医疗健康创新药
51CFO 判断:需深度理解biotech资本循环、临床管线估值建模、FDA/SEC双轨披露节奏及研发费用精细化管控。
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